Healing Genes

Sickle Cell awareness day June 19, 2021.
Why some are hopeful about CRISPR technology for SCD

First Person Treated for Sickle Cell Disease with CRISPR Doing Well The success of a Mississippi woman's treatment for sickle cell disease provides hope that gene editing could help treat the ailment

Our friends at Rare-X RARE-X are building the largest patient-driven, collaborative, open-data access project for rare diseases globally. visit

RARE-X is a collaborative platform for global data sharing for rare disease. We believe that rare patient communities, equipped to securely gather and share their data with collaborating researchers and companies around the globe, will significantly expand diversity and inclusion in research and dramatically accelerate progress across rare diseases.

Here's a story of resilience from Jake Javier who hit his head in a pool and broke his neck. He was a recipient of a special experimental treatment in a clinical trial using stem cells, and he regained function in his arms and legs.

VIDEO: Stem Cells and Spinal Cord Injury: A Patient's Perspective with Jake Javier An accident left Jake Javier paralyzed from the chest down the day before his high school graduation. Through a clinical trial, Javier received a transplant of 10 million stem cells and regained use of his arms and hands. Javier shares his story of resilience, science, and hope.